Mapping large numbers of results may take a few moments.
Search Results
Showing 1 - 9 of 9 results found.
Company | Activity | Company Description | Location | |
---|---|---|---|---|
Company AskBio | Activity: Research and Development | Company Description Asklepios BioPharmaceutical (AskBio) uses adeno-associated virus (AAV) technology to develop and manufacture gene therapies for rare diseases and other genetic disorders. | Location Research Triangle Park | |
Company Astellas Gene Therapies | Activity: Production and Manufacturing | Company Description Astellas Gene Therapies manufactures AAV gene therapy products for rare diseases. | Location Sanford | |
Company Kriya Therapeutics Inc. | Activity: Production and Manufacturing | Company Description Kriya Therapeutics develops AAV-based gene therapies for the treatment of type 1 and type 2 diabetes, severe obesity, thyroid eye disease (TED) and other indications. This location is the company's internal manufacturing facility. | Location Morrisville | |
Company Novartis Gene Therapies | Activity: Production and Manufacturing | Company Description Novartis Gene Therapies develops and commercializes gene therapies for patients and families devastated by rare and life-threatening neurological genetic diseases. The Durham site is Novartis Gene Therapies' manufacturing operations. | Location Durham | |
Company Pfizer Inc. (Durham) | Activity: Research and Development | Company Description Pfizer develops gene therapies to treat rare genetic central nervous system (CNS) and neuromuscular diseases. Pfizer's BioTherapeutics Pharmaceutical Sciences site in Durham houses clinical manufacturing space and analytical research development laboratories. | Location Durham | |
Company Pfizer Inc. (Sanford) | Activity: Production and Manufacturing | Company Description Pfizer's Sanford facility manufactures clinical trial and commercial materials for conjugate vaccines and gene therapies. | Location Sanford | |
Company Precision BioSciences Inc. (Durham) | Activity: Research and Development | Company Description Precision BioSciences is a clinical stage in vivo gene editing company using its novel ARCUS genome editing platform to develop new treatment options for genetic and infectious diseases. | Location Durham | |
Company Precision Biosciences Manufacturing Center for Advanced Therapeutics (RTP) | Activity: Production and Manufacturing | Company Description Precision BioSciences is a clinical stage in vivo gene editing company using its novel ARCUS genome editing platform to develop new treatment options for genetic and infectious diseases. | Location Research Triangle Park | |
Company Resilience (Durham) | Activity: Production and Manufacturing | Company Description Resilience manufactures viral vectors, a component of cell and gene therapies. | Location Durham |