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Showing 1 - 25 of 25 results found.
| Company | Activity | Company Description | Location | |
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Company AskBio | Activity: Research and Development | Company Description Asklepios BioPharmaceutical (AskBio) uses adeno-associated virus (AAV) technology to develop and manufacture gene therapies for rare diseases and other genetic disorders. | Location Research Triangle Park |
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Company Atsena Therapeutics Inc. | Activity: Research and Development | Company Description Atsena Therapeutics is developing ocular gene therapies to reverse or prevent blindness. | Location Durham |
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Company Azenta Life Sciences RTP | Activity: Contract Research and Testing | Company Description Azenta Life Sciences, formerly Genewiz, provides custom DNA sequencing, gene synthesis, genomics, next-generation sequencing and molecular biology in a GLP/cGMP regulatory environment. | Location Research Triangle Park |
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Company Bedrock Therapeutics Inc. | Activity: Research and Development | Company Description Bedrock Therapeutics is an AAV research and development company developing platform technologies and therapeutics. | Location Raleigh |
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Company BridgeBio Gene Therapy | Activity: Research and Development | Company Description BridgeBio Gene Therapy is developing a gene therapy for the treatment of a monogenic disease that presents in childhood. | Location Raleigh |
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Company CasTag Biosciences Inc. | Activity: Production and Manufacturing | Company Description CasTag Biosciences provides custom AAV kits. It uses CRISPR knock-in technology to produce genome-wide arrayed libraries with a variety of donors for endogenous protein analysis in cells and tissue. | Location Durham |
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Company CLAIRIgene LLC | Activity: Research and Development | Company Description CLAIRIgene develops viral vector platforms for gene therapy products to treat central nervous system diseases and conditions. | Location Durham |
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Company Creyon Bio | Activity: Research and Development | Company Description Creyon Bio is a drug development company engineering RNA-based medicines and their components. | Location Research Triangle Park |
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Company Enzerna Biosciences Inc. | Activity: Research and Development | Company Description Enzerna Biosciences is a pre-clinical stage company that is leveraging its proprietary RNA editing technology to develop long-term curative gene therapies for rare genetic disorders such as Huntington's Disease and Myotonic Dystrophy. | Location Morrisville |
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Company Epigenos Biosciences Inc. | Activity: Research and Development | Company Description Epigenos Biosciences develops personalized epigenome-based therapeutics that leverage site-specific DNA binding technologies to treat disease at the root of gene mis-regulation. | Location Morrisville |
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Company General Biosystems Inc. | Activity: Contract Research and Testing | Company Description General Biosystems provides gene synthesis, molecular biology, and protein expression and purification services. | Location Durham |
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Company GeneVentiv Therapeutics Inc. | Activity: Research and Development | Company Description GeneVentiv Therapeutics is a gene therapy company developing treatments for blood diseases and disorders, including treatments for Hemophilia A and B with or without inhibitors and for Hemophilia Arthropathy, a degenerative joint disease. | Location Raleigh |
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Company Inceptor Bio LLC | Activity: Research and Development | Company Description Inceptor Bio develops next-generation cell therapy platforms, across multiple cell types, to cure cancers. Its site includes a manufacturing facility for production of its therapies. | Location Raleigh |
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Company Isolere Bio Inc. | Activity: Research and Development | Company Description Isolere Bio is developing novel, non-chromatographic technologies for the purification of biologics such as antibodies, gene delivery vectors and personalized cell therapies. | Location Durham |
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Company Jaguar Gene Therapy LLC (Analytical Development) | Activity: Research and Development | Company Description Jaguar Gene Therapy develops gene therapies for patients suffering from severe genetic diseases. The company's analytical development lab is located in Durham. | Location Durham |
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Company Jaguar Gene Therapy LLC (Process Sciences Lab) | Activity: Research and Development | Company Description Jaguar Gene Therapy develops gene therapies for patients suffering from severe genetic diseases. The company's process sciences lab is located in Cary. | Location Cary |
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Company Kriya Therapeutics Inc. | Activity: Production and Manufacturing | Company Description Kriya Therapeutics develops AAV-based gene therapies for the treatment of type 1 and type 2 diabetes, severe obesity, thyroid eye disease (TED) and other indications. This location is the company's internal manufacturing facility. | Location Morrisville |
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Company Novartis Gene Therapies | Activity: Production and Manufacturing | Company Description Novartis Gene Therapies develops and commercializes gene therapies for patients and families devastated by rare and life-threatening neurological genetic diseases. The Durham site is Novartis Gene Therapies' manufacturing operations. | Location Durham |
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Company Pfizer Inc. (Durham) | Activity: Research and Development | Company Description Pfizer develops gene therapies to treat rare genetic central nervous system (CNS) and neuromuscular diseases. Pfizer's BioTherapeutics Pharmaceutical Sciences site in Durham houses clinical manufacturing space and analytical research development laboratories. | Location Durham |
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Company RainBio Inc. | Activity: Research and Development | Company Description RainBio is developing AAV (adeno-associated virus) gene therapy corneal treatments to address the unmet need of treatment of rare corneal blinding diseases. | Location Raleigh |
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Company Resilience (Durham) | Activity: Production and Manufacturing | Company Description Resilience manufactures viral vectors, a component of cell and gene therapies. | Location Durham |
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Company Sarepta Therapeutics Inc. (Durham) | Activity: Research and Development | Company Description Sarepta Therapeutics develops precision genetic medicine treatments for Duchenne muscular dystrophy (DMD), Limb-girdle muscular dystrophy (LGMD) and other central nervous system (CNS) disorders. Sarepta's Gene Editing Innovation Center is in Durham. | Location Durham |
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Company SNP Therapeutics LLC | Activity: Research and Development | Company Description SNP Therapeutics develops genetic tests to identify genetic variant patterns that contribute to disease. SNPT also designs nutritional therapeutics to treat metabolic disorders. | Location Kannapolis |
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Company Torque Bio Inc. | Activity: Research and Development | Company Description Torque Bio is a start-up leveraging the power of technology to develop novel gene therapies. | Location Durham |
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Company ViraSource LLC | Activity: Contract Research and Testing | Company Description ViraSource propagates and purifies BSL-1, BSL-2 viruses and bacteriophages. ViraSource also provides virus modifications and animal models of viral infections and antiviral immune responses. | Location Durham |