NCBiotech Company Directory

A comprehensive listing of North Carolina's life science industry

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Showing 1 - 26 of 26 results found.

Activity Company Description Location
Company AavantiBio (RTP) Activity: Research and Development Research and Development Company Description AavantiBio is developing novel gene transfer and gene editing therapies for the treatment of rare and ultra-rare genetic diseases. Location Research Triangle Park
Company Aceragen Inc. Activity: Research and Development Research and Development Company Description Aceragen is a clinical-stage biopharmaceutical company developing therapeutics for rare and orphan pulmonary and rheumatic diseases with high unmet medical need, including a late-stage therapy for Farber disease. Location Research Triangle Park
Company AMO Pharma Ltd. Activity: Research and Development Research and Development Company Description AMO Pharma is developing new treatments for serious and debilitating diseases including rare genetic disorders. Location Durham
Company Artiam Bio Inc. Activity: Research and Development Research and Development Company Description Artiam Bio is targeting the endocannabinoid system to treat diseases using pharmacology and medicinal chemistry approaches. Artiam Bio is initially focused on non-alcoholic and alcoholic liver diseases, Prader Willi syndrome and cannabis use disorder. Location Morrisville
Company AskBio Activity: Research and Development Research and Development Company Description Asklepios BioPharmaceutical (AskBio) uses adeno-associated virus (AAV) technology to develop and manufacture gene therapies for rare diseases and other genetic disorders. Location Research Triangle Park
Company Astellas Gene Therapies Activity: Production and Manufacturing Production and Manufacturing Company Description Astellas Gene Therapies manufactures AAV gene therapy products for rare diseases. Location Sanford
Company Baebies Inc. Activity: Production and Manufacturing Production and Manufacturing Company Description Baebies is a medical device company that develops and commercializes products to enable early disease detection and comprehensive diagnosis for children and adults. Location Durham
Company BridgeBio Gene Therapy Activity: Research and Development Research and Development Company Description BridgeBio Gene Therapy is developing a gene therapy for the treatment of a monogenic disease that presents in childhood. Location Raleigh
Company Chiesi USA Inc. Activity: Research and Development Research and Development Company Description Chiesi USA, the U.S. affiliate of Chiesi Farmaceutici S.p.A, develops and commercializes products in the therapeutic areas of rare disease, respiratory, cardiovascular, neonatology and cystic fibrosis. Location Cary
Company Collaborations Pharmaceuticals Inc. Activity: Contract Research and Testing Contract Research and Testing Company Description Collaborations Pharmaceuticals develops drugs for rare and neglected diseases using machine learning software, providing preclinical and clinical expertise to rare disease foundations, academic scientists and companies developing clinical candidates. Collaborations also provides machine learning expertise and software to consumer product and agrochemical companies. Location Raleigh
Company Couragen Biopharmaceutics LLC Activity: Research and Development Research and Development Company Description Couragen Biopharmaceutics develops gene and protein therapy products for preclinical and clinical use for the treatment of genetic and chronic diseases. Couragen also provides custom adeno-associated virus vectors as a tool for laboratory research. Location Chapel Hill
Company DuraBull Pharmaceuticals Inc. Activity: Research and Development Research and Development Company Description DuraBull Pharmaceuticals develops medical therapies for patients with hereditary aortopathy. Location Durham
Company Enzerna Biosciences Inc. Activity: Research and Development Research and Development Company Description Enzerna Biosciences is a pre-clinical stage company that is leveraging its proprietary RNA editing technology to develop long-term curative gene therapies for rare genetic disorders such as Huntington's Disease and Myotonic Dystrophy. Location Morrisville
Company Enzyvant Inc. Activity: Research and Development Research and Development Company Description Enzyvant, a subsidiary of Sumitovant Biopharma, develops regenerative therapeutics for rare diseases such as congenital athymia. Location Durham
Company Genencine Therapeutics LLC Activity: Research and Development Research and Development Company Description Genencine Therapeutics develops mRNA vaccines for the prevention and treatment of cancer, viral diseases and autoimmune diseases, as well as mRNA therapeutic drugs for genetic diseases. Location Durham
Company Glycomine Inc. Activity: Research and Development Research and Development Company Description Glycomine is developing orphan drugs for serious rare disorders of metabolism and protein misfolding. Location Chapel Hill
Company Jaguar Gene Therapy LLC Activity: Research and Development Research and Development Company Description Jaguar Gene Therapy develops gene therapies for patients suffering from severe genetic diseases. Location Cary
Company Juno Metabolomics LLC Activity: Production and Manufacturing Production and Manufacturing Company Description Juno Metabolomics is developing next-generation metabolomics for precision medicine. Location Chapel Hill
Company MitoRainbow Therapeutics Inc. Activity: Research and Development Research and Development Company Description MitoRainbow is developing treatments for TK2 deficiency, a mitochondrial disease that manifests as severe myopathy. Location Cary
Company ML Bio Solutions Inc. Activity: Research and Development Research and Development Company Description ML Bio Solutions is developing an oral treatment for patients with limb girdle muscular dystrophy 2i. Location Charlotte
Company NeuroGT Inc. Activity: Research and Development Research and Development Company Description NeuroGT is developing gene therapy products to treat rare neurogenetic diseases. Location Chapel Hill
Company Novartis Gene Therapies Activity: Production and Manufacturing Production and Manufacturing Company Description Novartis Gene Therapies develops and commercializes gene therapies for patients and families devastated by rare and life-threatening neurological genetic diseases. The Durham site is Novartis Gene Therapies' manufacturing operations. Location Durham
Company QOL Medical LLC Activity: Sales and Operations Sales and Operations Company Description QOL Medical commercializes existing and complementary new orphan products for metabolic disease and pediatric gastroenterology. Location Raleigh
Company Rescindo Therapeutics Inc. Activity: Research and Development Research and Development Company Description Rescindo Therapeutics, Inc. is a drug discovery & development company focused on rare genetic diseases, especially those affecting children. Location Cary
Company Resilience (Durham) Activity: Production and Manufacturing Production and Manufacturing Company Description National Resilience manufactures lentiviral vectors, a component of cell and gene therapies. Location Durham
Company Tellus Therapeutics Inc. Activity: Research and Development Research and Development Company Description Tellus Therapeutics is developing novel small molecules derived from human maternal breast milk for the treatment of newborns with perinatal brain injury. Location Hillsborough